Tag: Gene therapy
Genetic and Health Data Analyses of Finnish Biobank Participants Describe Hundreds of Novel Genetic...
Since initiation in 2017, the FinnGen study has developed into one of the world’s leading biobank-based genomic research projects. Currently FinnGen is completing the construction of a resource that integrates genomic information from 500,000 Finns with more than half...
Ultra-low Temperature Freezers Have Become Important for Today’s Cell and Gene Therapies
Ultra-Low Temperature Freezers (ULTs) can make an important contribution in the field of cell and gene therapies. For a long time, complex cryopreservation with liquid nitrogen was the standard for freezing all therapeutic substances. However, studies show that some...
New AI Method Makes it Possible to Analyse Cancer Genomes from FFPE Tissue Samples
Scientists have developed an artificial intelligence (AI) method that could unlock a research ‘treasure trove’ of cancer genomes from billions of preserved tissue samples stored routinely at hospitals over decades. The new method makes it possible for the first time...
Using Ultra-Low Freezers to Maintain the Viability of Cell and Gene Therapy Products
Many cell and gene therapy solutions have shown considerable promise as a source of possible treatments for a wide range of chronic disorders. However, these sophisticated therapies introduce additional barriers such as the requirements for ultra-low and cryogenic storage,...
Phenomix Sciences Announces First Obesity Biobank Registry to Study Underlying Phenotypes
On a mission to conquer obesity, Phenomix Sciences has launched its first obesity biobanking registry and outcomes study. The registry will study variability in obesity by looking at genetic and environmental factors in patients, and analyze interventions that will...
CRISPR Therapeutics And Vertex Release Interim Phase I Data On CRISPR/Cas9 Gene-Editing Therapy
CRISPR Therapeutics and Vertex Pharmaceuticals Incorporated have
announced positive, interim data from the first two patients with severe
hemoglobinopathies treated with the investigational CRISPR/Cas9 gene-editing
therapy CTX001 in ongoing Phase 1/2 clinical trials. One patient with
transfusion-dependent beta thalassemia (TDT) received CTX001 in...
Biobanking Science: CRISPR Gene Editing to Treat Human Disease
This year has seen a flurry of good news about CRISPR gene editing clinical trials in human patients. CRISPR-Cas 9 is a gene editing tool capable of providing specific changes to genes in a wide range of animal models....
BioLife Solutions Positive About FDA’s Proposed New Policies To Advance Cell And Gene Therapies
BioLife Solutions, Inc., has announced that the company expects to benefit from the new policies to advance the development of safe and effective cell and gene therapies as set forth in a statement issued by the U.S. Food and...
Biobanking Science: Safe Gene Therapy
Gene therapy has the potential to cure any disease caused by genetic mutations. For gene therapy to work, normal copies of genetic DNA, replacement messenger RNA or gene-editing constructs must be delivered to affected cells. Nucleic acids are rapidly...
Key Biologics And Astarte Biologics Merge, Ampersand Funds Expansion Of Cell And Gene Therapy
Key Biologics, founded in 2009, headquartered in Memphis, Tennessee, provides research and clinical grade human cells and blood products and related services to pharmaceutical, biotech, medical device and academic institutions around the world. The company is focused on advancing...
